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Table 3 Standardized compounded medication commonly prescribed for rare diseases

From: Compounded medication for patients with rare diseases

Compounded Medication

Information Source

Beta-Carotene 30 mg & 100 mg capsules

TMF

Cafeine without citrate 1% 10 ml injection

OpenAPO

Cafëine-citraat 20 mg/2 ml injection

BP, FNA, IJPC

Chenodeoxycholic acid 250 mg capsules

TMF

Ciclosporin 2% eye drops

IJPC

Cysteamine 0,15% & 0,5% eye drops

DAC, FFP

Glycopyrrolate 0,5 mg/ml oral suspension

CT, Fagron, IJPC, IWK, NZ

Hydroxocobalamine 0,1% 10 ml injection

BP, OpenAPO

Levo-Arginine HCl 100 mg/ml 50 ml injection

FNA

Levo-Arginine HCl 100 mg/ml oral liquid

TMF

Levo-Carnitine 200 mg/ml oral liquid

CT, TMF

Midazolam 0,5% nasal spray

FFP

Midazolam 2,5% nasal spray

OpenAPO

Penicillamine 50 mg/ml oral suspension

Fagron

Polihexanide 0,02% eye drops

OpenAPO

Potassium−/sodiumcitrate oral liquid

FNA (prep), IJPC

Potio Joulie (disodium hydrogenphosphate) oral liquid

HUG, IJPC

Primaquine phosphate 30 mg capsules

TMF

Primaquine phosphate 6 mg/5 ml oral suspension

MPA

Propranolol 1 mg/ml oral suspension

Fagron, FFP, IJPC, IWK, SEFH

Propranolol 5 mg/ml oral suspension

CHEO, FPP, NZ

Pyridoxal phosphate 10 mg capsules

TMF

Pyridoxal phosphate 25 mg/ml oral suspension

NC

Riboflavin 10 mg/ml oral suspension

CRI, Fagron

Sildenafil Citrate 2,5 mg/ml oral suspension

CHEO, IWK, MPA, NZ, SEFH, USP40

Sodium benzoate 100 mg/ml oral liquid

TMF

Sodium dihydrogen phosphate 156 mg/ml oral liquid

CT, FNA

Sodium phenylbutyrate 200 mg/ml oral liquid

IJCP, TMF, USP40

Sodium thiosulphate injection

BP

Ursodeoxycholic acid suspension 15 mg/ml oral suspension

FFP

Ursodeoxycholic acid suspension 20 mg/ml oral suspension

IWK, MPA, NC

Ursodeoxycholic acid suspension 50 mg/ml oral suspension

CHEO, CRI, NZ, USP40