Patient characteristics | |||
---|---|---|---|
MPS I | N | MPS III | N |
Total number of patients | 29 | Total number of patients | 46 |
Male | 15 | Male | 27 |
Female | 14 | Female | 19 |
MPS I phenotype | MPS III subtype | ||
Hurler | 20 | MPS IIIA | 28 |
Non-Hurler | 9 | MPS IIIB | 9 |
MPS IIIC | 9 | ||
MPS III phenotype | |||
Rapidly progressing (RP) MPS III | 16 | ||
Slowly progressing (SP) MPS III | 28 | ||
Unknown | 1 |