SMA type
|
Estimated prevalencea
|
Estimated prevalenceb
|
---|
I
|
1764
|
1293
|
II
|
4322
|
4035
|
III
|
4247
|
4247
|
All
|
10,333
|
9575
|
-
SMA spinal muscular atrophy
-
aUsed published survival estimates from US literature only
-
bUsed combined published survival estimates from the United States, Europe, and Australia