SMA type
|
Estimated prevalencea
|
Estimated prevalenceb
|
---|
I
|
1455
|
1067
|
II
|
3567
|
3330
|
III
|
3504
|
3504
|
All
|
8526
|
7901
|
-
SMA spinal muscular atrophy
-
aUsed published survival estimates from US literature only
-
bUsed combined published survival estimates from the United States, Europe, and Australia