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Table 1 Results of Analyses

From: Do investors value the FDA orphan drug designation?

Study

Cumulative Abnormal Returns (CARs)

GRANK-T Test Statistic (p-value)

Analysis 1 (n = 323)

3.36%

2.41 a (0.992)

Analysis 2

  

 Oncology (n = 169)

3.78%

2.07 a (0.976)

  1985–2005 (n = 67)

3.47%

1.09 (0.862)

  2006–2015 (n = 102)

3.98%

1.73 (0.958)

 Non-oncology (n = 154)

2.91%

1.57 (0.942)

  1985–2005 (n = 67)

3.28%

2.17 a (0.985)

  2006–2015 (n = 87)

2.62%

0.86 (0.805)

Analysis 3

  

 Nano-cap: Market cap <$50 m (n = 40)

8.87%

1.02 (0.846)

 Micro-cap: Market cap >$50 m & < $250 m (n = 94)

4.25%

1.50 (0.933)

 Small-cap: Market cap >$250 m & < $2b (n = 92)

0.15%

0.40 (0.655)

 Mid- & Large-cap: Market cap >$2b (n = 21)

−0.20%

−0.17 (0.433)

  1. astatistically significant at the 5% level