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Table 1 Generalized Estimating Equation Regression Results for Health State Utility in Gaucher Disease Type 1

From: A new framework for evaluating the health impacts of treatment for Gaucher disease type 1

  Mean or Proportion for estimation sample Coefficient Robust standard error 95% CI
DS3 Severity (vs. Mild)
 Moderate 0.381 −0.078** 0.037 −0.150, −0.005
 Marked 0.113 −0.122*** 0.042 −0.205, −0.039
 Severe 0.021 −0.168** 0.055 −0.275, −0.061
Bone Pain 0.258 −0.098*** 0.034 −0.165, −0.032
Severe Skeletal Complications 0.103 0.018 0.037 −0.055, 0.090
Female 0.691 −0.049 0.030 −0.108, 0.010
Age at Treatment Initiation 53.9 −0.002* 0.001 −0.004, 0.001
Constant   0.880*** 0.078 0.727, 1.033
Number of Observations 97    
Number of Patients 50    
  1. ***p < 0.01, **p < 0.05, *p < 0.10
  2. Abbreviations: CI confidence interval, DS3 disease severity scoring system