Table 5 Reason for study termination
From: Clinical course of 63 patients with neonatal onset urea cycle disorders in the years 2001–2013
Reason for study termination | CPS1D | OTCD | ASSD | All patients |
|---|---|---|---|---|
Number of patients | 12 | 23 | 27 | 63a |
Death | 4 (33.3 %) | 10 (43.5 %) | 4 (14.8 %) | 18 (28.6 %) |
Liver cell infusion | – | 1 (4.3 %) | – | 1 (1.6 %) |
Orthotopic liver transplantation (OLT) | 2# (16.7 %) | 5 (21.7 %) | 4 (14.8 %) | 11 (17.5 %) |
Study end | 6 (50.0 %) | 7 (30.4 %) | 19 (70.4 %) | 33 a (52.4 %) |