No. | Drug-indication pair | Indication uniqueness | Disease rarity | Disease severity | Adv.tech. | Manufacturing technology | Therapeutic alternative | Sci. evid. clin.eff. | Benefits from use of medicine | Total number of points |
---|---|---|---|---|---|---|---|---|---|---|
1 | Elaprase | 2 | 2 | 1 | 2 | 2 | 2 | 1 | 1 | 13 |
2 | Fabrazyme | 2 | 2 | 2 | 2 | 2 | 0 | 1 | 1 | 12 |
 | THRESHOLD | 75 % |  |  |  |  |  |  |  | 12 points |
3 | Nexavar (HCC) | 1 | 2 | 2 | 0 | 2 | 2 | 2 | 0 | 11 |
4 | Kuvan | 0 | 2 | 1 | 1 | 2 | 2 | 1 | 2 | 11 |
5 | Nplate | 2 | 1 | 0 | 2 | 2 | 2 | 1 | 1 | 11 |
6 | Cystadane | 2 | 2 | 2 | 0 | 0 | 2 | 0 | 2 | 10 |
7 | Yondelis | 1 | 1 | 2 | 2 | 0 | 2 | 2 | 0 | 10 |
8 | Somavert | 2 | 1 | 1 | 2 | 2 | 0 | 1 | 1 | 10 |
9 | Tasigna | 2 | 2 | 2 | 0 | 0 | 2 | 1 | 1 | 10 |
10 | Increlex | 2 | 0 | 0 | 2 | 2 | 2 | 1 | 1 | 10 |
11 | Glivec – (GIST) | 0 | 2 | 2 | 0 | 1 | 2 | 2 | 0 | 9 |
12 | Revlimid (MM/S) | 1 | 0 | 2 | 1 | 0 | 2 | 2 | 1 | 9 |
13 | Glivec (DFSP) | 0 | 2 | 2 | 0 | 1 | 2 | 1 | 1 | 9 |
14 | Torisel | 1 | 0 | 2 | 2 | 2 | 0 | 1 | 1 | 9 |
15 | Ventavis | 2 | 0 | 1 | 1 | 2 | 0 | 1 | 1 | 8 |
16 | Zavesca | 1 | 1 | 2 | 1 | 0 | 0 | 1 | 2 | 8 |
17 | Tracleer | 1 | 1 | 1 | 0 | 2 | 0 | 1 | 2 | 8 |
18 | Volibris | 2 | 2 | 0 | 1 | 0 | 0 | 1 | 2 | 8 |
19/20 | Nexavar (RCC) | 1 | 0 | 2 | 0 | 2 | 1 | 2 | 0 | 8 |
 | THRESHOLD | 50 % |  |  |  |  |  |  |  | 8 points |
21 | Vidaza | 1 | 0 | 2 | 1 | 0 | 0 | 2 | 1 | 7 |
22 | Sprycel | 1 | 1 | 2 | 0 | 0 | 1 | 1 | 1 | 7 |
23 | Revlimid (MM) | 1 | 0 | 2 | 1 | 0 | 0 | 2 | 1 | 7 |
24 | Atriance | 1 | 0 | 2 | 1 | 0 | 2 | 1 | 0 | 7 |
25 | Glivec (ALL Ph+) | 0 | 1 | 2 | 0 | 1 | 0 | 1 | 0 | 5 |
26 | Revatio | 0 | 1 | 1 | 0 | 0 | 0 | 1 | 2 | 5 |
27 | Glivec (MDS/MPD) | 0 | 0 | 2 | 0 | 1 | 0 | 1 | 0 | 4 |
 | THRESHOLD | 25 % |  |  |  |  |  |  |  | 4 points |