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Fig. 2 | Orphanet Journal of Rare Diseases

Fig. 2

From: Early treatment with laronidase improves clinical outcomes in patients with attenuated MPS I: a retrospective case series analysis of nine sibships

Fig. 2

Physician-rated Severity of Symptoms at T1 and T2. Figure 2 Severity of Symptoms at T1 and T2. Severity of key clinical symptoms for older and younger siblings in at the initiation of ERT (T1) and at follow-up (T2) was rated by physicians. Results are organized by group and coded by color. Symptoms were absent, or ranged in severity from mild to severe

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172