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Table 1 Patient characteristics at baseline

From: A conceptual disease model for adult Pompe disease

Number of patients N Mean Min Max
Age (years) 79 49.3 23.0 72.6
Gender (female) 79 50.6 %   
Duration since diagnosis (years) 79 8.0 0.0 27.5
Enzyme activity (% of normal) 79 12.4 0.5 19.9
Muscle strength (% predicted) 64 82.1 48.3 100.0
Respiratory function (% predicted) 63 76.1 11.3 123.4
Fatigue Severity Scale 61 5.6 2 7
Rotterdam Handicap Scale 64 27.4 13.5 36.0
Visual Analogue Scale 49 65.0 30.0 95.0
Mental Component Scale 60 53.8 24.2 74.0
Physical Component Scale 60 35.4 17.6 53.3
EQ-5D Utility 50 0.736 0.201 1.000