Patient no. | Phenotype | Age at start of ERT (Yrs) | Age at assessment of antibody status | Antibody titre | Cellular uptake inhibition % | Inhibitory antibodies beyond 1Â year |
---|---|---|---|---|---|---|
1 | Hurler | 11 | 13* | 262336 | 86.1 | Yes* |
2 | Hurler | 7 | 7 | 65536 | 41.8 | No |
3 | Hurler | 6 | 7 | 262144 | 88.3 | Yes |
4 | Hurler-Scheie | 5 | 7* | 262336 | 0 | No |
5 | Hurler-Scheie | 4 | 4* | 32768 | 33.0 | Yes* |
6 | Hurler-Scheie | 5 | 13* | 32768 | 95.4 | Yes* |
7 | Hurler-Scheie | 8 | 15 | 256 | 0 | No |
8 | Hurler-Scheie | 6 | 13* | 512 | 0 | No |
9 | Hurler-Scheie | 3 | 9* | 1 | n/a | No |
10 | Hurler-Scheie | 3 | 10* | 256 | 0 | No |
11 | Hurler-Scheie | 7 | 14* | 1 | n/a | No |
12 | Hurler-Scheie | 12 | 12 | 4096 | 0 | No |
13 | Hurler-Scheie | 2 | 7* | 1 | n/a | No |
14 | Hurler-Scheie | 4 | 4 | 32768 | 25.5 | No |
15 | Hurler-Scheie | 4 | 7* | 256 | 30.09 | No |
16 | Hurler-Scheie | 4 | 7* | 32 | 1 | No |
17 | Scheie | 30 | 30 | 131072 | 58.10 | No |
18 | Scheie | 27 | 28* | 262144 | 30.12 | Yes* |
19 | Scheie | 15 | 15 | 4096 | 11.6 | No |
20 | Scheie | 9 | 10* | 2048 | 31.4 | No |