Figure 1From: Long term follow-up to evaluate the efficacy of miglustat treatment in Italian patients with Niemann-Pick disease type C Evolution over time of the mean composite severity score (MCSS) of neurologically symptomatic patients during miglustat treatment. Patients with a) adult (n = 6), b) juvenile (n = 10), c) late infantile (n = 5) and d) early infantile (n = 2) phenotypes.Back to article page