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Table 2 Response rate and age distribution within the analyzed patient cohort

From: Comparative cost of illness analysis and assessment of health care burden of Duchenne and Becker muscular dystrophies in Germany

  DMD BMD
Total I II III IV V Total I II III IV V
Response rate   
Absolute numbers 248/571 49 70 11 92 26 115/162 42 55 8 10 0
Ratio of total DMD/BMD [%] 43 20 28 4 37 11 71 37 48 7 9 0
Respondents patients/parents [%] 10/90 68/32
Age of patients   
Min. [years] 1 1 3 10 1 11 2.5 2.5 7 7 21 -
Max. [years] 42 14 42 23 31 40 62 52 59 41 62 -
Median [years] 11 4 7.5 13 16 22.5 26.5 16 33 30 51 -
  1. Response rates and age distribution were differentiated based on clinical severity stages. Because of rounding, percentage might not add up to exactly 100%.