Trade name | Active substance | Indication | Reimbursement |
---|---|---|---|
Afinitor* | Everolimus | Neuroendocrine tumours of pancreatic origin (pNET) | Â |
Renal cell carcinoma (RCC) | |||
Aldurazyme* | Laronidase | Mucopolysaccharidosis I (MPS I) | CCUH |
Arzerra | Ofatumumab | CLL | Individual |
Atriance | Nelarabine | T-cell ALL | Individual |
T-cell lymphoblastic lymphoma | |||
Carbaglu | Carglumic acid | Hyperammonaemia | Â |
Cystadane | Betaine anhydrous | Homocystinuria | CCUH/Individual |
Diacomit | Stiripentol | Severe myoclonic epilepsy in infancy (Dravet’s syndrome) | Individual |
Elaprase | Idursulfase | MPS II (Hunter syndrome) | CCUH |
Evoltra | Clofarabine | ALL | Â |
Exjade | Deferasirox | Beta thalassaemia major with iron overload due to blood transfusion | Individual |
Gliolan | 5-aminolevulinic acid hydrochloride | Malignant glioma | Â |
Glivec* | Imatinib | Ph + CML | List A |
GIST | (previously list C) | ||
Dermatofibrosarcoma protuberans | Individual | ||
Ph + ALL | |||
Hypereosinophilic syndrome | |||
Myelodysplastic/ myeloproliferative diseases | |||
Increlex | Mecasermin | Primary insulin-like growth factor 1 deficiency | CCUH |
Jakavi | Ruxolitinib | Myelofibrosis | Â |
Kuvan | Sapropterin | Phenylketonuria | CCUH |
Tetrahydrobiopterin deficiency | |||
Litak | Cladribine | Hairy cell leukaemia | Â |
Mozobil | Plerixafor | Haematopoietic stem cell transplantation in lymphoma or multiple myeloma patients | Individual |
Myozyme | Alglucosidase alpha | Pompe disease | Â |
Nexavar | Sorafenib | Hepatocellular carcinoma | Individual |
RCC | |||
Nplate | Romiplostim | ITP | Individual |
Orfadin | Nitisinone | Hereditary tyrosinaemia type 1 | Â |
Pedea | Ibuprofen | Patent ductus arteriosus in preterm newborns | Â |
Peyona | Caffeine citrate | Primary apnea of premature newborns | Â |
Revatio | Sildenafil | PAH | Individual |
Revolade* | Eltrombopag | ITP | Individual |
Sprycel | Dasatinib | Ph + CML | List C |
Ph + ALL | Individual | ||
Sutent* | Sunitinib | GIST | Individual |
RCC | |||
pNET | |||
Tasigna | Nilotinib | Ph + CML | List C |
Tobi Podhaler | Tobramycin | Pseudomonas aeruginosa infection in cystic fibrosis patients | Â |
Ventavis* | Iloprost | PAH | Â |
Volibris | Ambrisentan | PAH | Individual |
Votubia | Everolimus | Renal angiomyolipoma or subependymal giant cell astrocytoma associated with tuberous sclerosis complex | Â |
Wilzin | Zinc acetate dihydrate | Wilson’s disease | Individual |
Yondelis | Trabectedin | Soft tissue sarcoma | Â |
Ovarian cancer |