Cardiac variant, IVS4ā+ā919Gā>āA FD patients | Parameters, patient number | Baseline (MeanāĀ±āSD) | After ERT (MeanāĀ±āSD) | P value |
---|---|---|---|---|
Male | LVMI (g/H2.7) Nā=ā16 | 81.1āĀ±ā32.2 | 71.0āĀ±ā25.6 | 0.016* |
Compare between baseline and 1st Lyso-Gb3 (nM) Nā=ā16 | 8.5āĀ±ā3.3 | 6.7āĀ±ā2.2 | 0.012* | |
Compare between baseline and the last Lyso-Gb3 (nM) Nā=ā16 | 8.5āĀ±ā3.3 | 7.4āĀ±ā2.8 | 0.163 | |
Female | LVMI (g/H2.7) Nā=ā7 | 59.4āĀ±ā12.8 | 42.0āĀ±ā10.2 | <0.001* |
Compare between baseline and 1st Lyso-Gb3 (nM) Nā=ā7 | 2.6āĀ±ā1.0 | 1.2āĀ±ā0.9 | 0.018* | |
Compare between baseline and the last Lyso-Gb3 (nM) Nā=ā7 | 2.6āĀ±ā1.0 | 2.6āĀ±ā1.6 | 0.938 |