|
Half-life of response (years)
|
0.5 (0.01-3.1)
| |
|
Time to 95% of response (years)
|
2.1 (0.4-13.4)
| |
|
Ratio (level at steady state/level at ERT initiation)
| | |
|
Ferritin (%)
|
38.1 (2.1-101.5)
| |
|
Chitotriosidase (%)
|
10.1 (0.8-116.7)
| |
|
Hemoglobin (%)
|
117.3 (88.6-173.1)
| |
|
Platelets (%)
|
200.4 (83.5-437.8)
| |
|
Predicted value at steady state
| | |
|
Ferritin (μg/L)
|
202.0 (16.5-1280.1)
|
115 (58.4)
|
|
Chitotriosidase (nmol/h.mL)
|
820 (8–18183)
|
131 (66.5)
|
|
Hemoglobin (g/dL)
|
13.5 (8.1-17.2)
|
174 (88.3)
|
|
Platelets (/mm3)
|
172 000 (48 000–526 000)
|
126 (64.0)
|
