ST | ERT | Difference | [95% confidence interval] | |
---|---|---|---|---|
Life expectancy (years) | 0.40 | 13.79 | 13.39 | [1.55 – 25.23] |
QALYs | 0.24 | 7.00 | 6.75 | [2.32 – 11.19] |
Total costs | € 32,871 | € 7,032,899 | € 7,000,028 | [1,869,635 – 12,130,422] |
- ERT costs | € - | € 6,630,525 | € 6,630,525 | [1,615,059 – 11,645,991] |
- Infusion costs | € - | € 212,793 | € 212,793 | [121,477 – 304,108] |
- Other costs | € 32,871 | € 189,582 | € 156,711 | [131,728 – 181,694] |