Skip to main content

Table 4 Simple linear regression analysis

From: Shining a light in the black box of orphan drug pricing

 

Belgium n = 51

France n = 59

Netherlands n = 52

Czech Republic n = 41

Italy n = 28

United Kingdom n = 66

Variable (x)

logBeATXcost=

p-value

logFrATXcost=

p-value

logNlATXcost=

p-value

logCzATXcost=

p-value

logItATXcost=

p-value

logUkATXcost=

p-value

Cosize

4.422-0.214x

0.329

4.449-0.175x

0.360

4.033 + 0.258x

0.176

4.647-0.520x

0.015*

4.534-0.228x

0.477

4.505-0.115x

0.465

ONCO

4.290 + 0.007x

0.973

4.321 + 0.081x

0.677

4.000 + 0.313x

0.107

4.270 + 0.203x

0.361

4.573-0.326x

0.305

4.414 + 0.040x

0.804

YAUTH

4.584-0.042x

0.406

4.664-0.049x

0.220

4.396-0.044x

0.196

4.765-0.060x

0.267

4.519-0.006x

0.942

4.665-0.039x

0.204

AvailUS

3.837 + 0.600x

0.014*

3.829 + 0.661x

0.004*

3.967 + 0.242x

0.234

4.078 + 0.399x

0.104

3.973 + 0.543x

0.328

4.240 + 0.250x

0.189

MultipleIND

4.159 + 0.558x

0.024*

4.142 + 0.645x

0.001*

3.980 + 0.760x

0.001*

4.277 + 0.277x

0.241

4.277 + 0.595x

0.047*

4.292 + 0.455x

0.007*

REPUR

4.473-0.816x

0.001*

4.495-0.684x

0.003*

4.324-0.711x

0.000*

4.502-0.771x

0.006*

4.505-0.793x

0.303

4.558-0.545x

0.003*

QoLimp

4.239 + 0.451x

0.171

4.248 + 0.556x

0.019*

4.066 + 0.535x

0.069

4.313 + 0.427x

0.200

4.313 + 0.628x

0.052

4.368 + 0.348x

0.090*

Survimp

4.242 + 0.321x

0.274

4.344 + 0.069x

0.803

4.048 + 0.592x

0.031*

4.255 + 0.497x

0.057

4.424 + 0.350x

0.394

4.391 + 0.206x

0.303

dbRCT

4.341-0.089x

0.682

4.389-0.068x

0.724

4.265-0.278x

0.146

4.562-0.390x

0.074

4.435-0.085x

0.772

4.440-0.017x

0.915

altTX

5.000-0.883x

0.001*

4.919-0.782x

0.000*

4.471-0.436x

0.059

4.958-0.676x

0.039*

5.098-0.988x

0.000*

4.906-0.669x

0.000*

Ultrarare

4.200 + 0.303x

0.171

4.245 + 0.295x

0.132

4.132 + 0.163x

0.420

4.381 + 0.086x

0.752

4.281 + 0.353x

0.249

4.347 + 0.193x

0.249

Chronic

3.883 + 0.554x

0.021*

3.954 + 0.493x

0.040*

3.963 + 0.228x

0.289

4.310 + 0.073x

0.785

3.947 + 0.620x

0.124

4.114 + 0.414x

0.027*

Weightbased

4.185 + 0.216x

0.315

4.289 + 0.142x

0.458

4.231-0.209x

0.276

4.222 + 0.305x

0.167

4.346 + 0.351x

0.242

4.321 + 0.235x

0.143

Oral

4.563-0.500x

0.018*

4.609-0.449x

0.017*

4.154-0.040x

0.840

4.650-0.540x

0.012*

4.705-0.411x

0.156

4.623-0.400

0.011*

  1. Explanatory variables are described in Table 2. N denotes the number of observations. All p-values marked in bold with an asterisk are significant at a 0.05 threshold level. ATXcost = annual treatment cost.