Skip to main content

Table 2 Mean VABS Total Score by Visit (ITT Population)

From: Intra-Erythrocyte Infusion of Dexamethasone Reduces Neurological Symptoms in Ataxia Teleangiectasia Patients: Results of a Phase 2 Trial

 

Mean (SD)

95% CI for the mean

MeanΔ (SD)

95% CI for meanΔ

Median

Min-max

p-value*

V1

5.5 (2.0)

(4.7/6.3)

-

 

5.1

2.1–11.0

-

V4

6.5 (2.1)

(6/7.8)

1.0 (0.9)

(0.7/1.5)

6.2

3.6–10.9

<0.0001

V7

6.9 (2.3)

(6/8)

1.3 (1.2)

(0.8/1.8)

6.9

2.5–11.1

<0.0001

  1. *Comparison vs. baseline (V1) using Wilcoxon non-parametric test.
Back to article page

Orphanet Journal of Rare Diseases

ISSN: 1750-1172