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Table 4 Treatment Status of 91 South Florida GD1 patients as of the most recent evaluation through June 2011*

From: Patients with type 1 Gaucher disease in South Florida, USA: demographics, genotypes, disease severity and treatment outcomes

 

No. of pts

ERT dose (Units/kg)

Treatment status

 

<30

30-45

46-60

>60

Never treated

15

    

Imiglucerase (total)

49

    

  Q1W

   

1

 

  Q2W

 

3

14

16

 

  Q3W

   

2

 

  Q4W

  

1

9

3

Velaglucerase alfa (total

10

    

  Q2W

  

2

6

 

  Q3W

    

1

  Q4W

   

1

 

Miglustat 100 mg po TID

4

    

Treatment interrupted and not resumed (total)

13

    

  Severe infusion reactions

3

    

  Treatment shortage

10

    
  1. *Two patients with unknown genotypes who were treated solely with alglucerase prior to 1994 are excluded from this analysis.