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Table 4 Treatment Status of 91 South Florida GD1 patients as of the most recent evaluation through June 2011*

From: Patients with type 1 Gaucher disease in South Florida, USA: demographics, genotypes, disease severity and treatment outcomes

  No. of pts ERT dose (Units/kg)
Treatment status   <30 30-45 46-60 >60
Never treated 15     
Imiglucerase (total) 49     
  Q1W     1  
  Q2W   3 14 16  
  Q3W     2  
  Q4W    1 9 3
Velaglucerase alfa (total 10     
  Q2W    2 6  
  Q3W      1
  Q4W     1  
Miglustat 100 mg po TID 4     
Treatment interrupted and not resumed (total) 13     
  Severe infusion reactions 3     
  Treatment shortage 10     
  1. *Two patients with unknown genotypes who were treated solely with alglucerase prior to 1994 are excluded from this analysis.