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Table 4 Applicable individuals for exon 51 skipping clinical trial

From: Characteristics of Japanese Duchenne and Becker muscular dystrophy patients in a novel Japanese national registry of muscular dystrophy (Remudy)

Deleted exons

No. of individuals

% in registrants

45-50

17

2.9%

47-50

0

0.0%

48-50

9

1.5%

49-50

18

3.1%

50

6

1.0%

52

7

1.2%

52-63

0

0.0%

total

57

9.8%

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172