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Figure 1 | Orphanet Journal of Rare Diseases

Figure 1

From: Impact of enzyme replacement therapy on survival in adults with Pompe disease: results from a prospective international observational study

Figure 1

Adjusted Hazard Ratios of the Different Models Describing the Relationship Between ERT and Survival. Model 1a: Intent-to-treat approach with enzyme replacement therapy (ERT), age categories, and disease severity as time-dependent covariates. Model 2a: Intent-to-treat approach with only ERT as time-dependent covariate. Model 1b: Analysis excluding person-time after discontinuation of treatment with ERT, age categories, and disease severity as time-dependent covariates. Model 2b: Analysis excluding person-time after discontinuation of treatment with only ERT as time-dependent covariate.

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Orphanet Journal of Rare Diseases

ISSN: 1750-1172