Database information
|
Families of SMA
|
International IU FSMA Registry
|
MDA
|
Treat-NMD
|
Estimated
|
---|
Number of patients
|
11,000
|
3,000
|
5,500
|
2,400
| |
SMA subtypes (%)
|
I* 51
|
I 28
|
I 19.1
|
I 20
|
I 60
|
|
II* 24
|
II 33.5
|
II 35.4
|
II 43
|
II 30
|
|
III* 12
|
III 26
|
III 28.8
|
III 37
|
III 10
|
|
IV/Unknown* 13
| |
IV 16.7
| | |
Average age of diagnosis (months)
|
I 4.9
| | | | |
II 18.7
|
Average age at entry into registry (months)
|
I 6
| | | | |
II 20
|
- *Calculated from approximately 1,000 newly diagnosed patients contacting FSMA over the previous three-year period (Courtesy of Families of SMA).