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Table 1 Mean health utilities per year by disease state cluster and 95% confidence intervals after boots-trapping

From: Cost-effectiveness of enzyme replacement therapy for Fabry disease

  N* Mean health utility 95% LCL 95% UCL
Asymptomatic 19 0.874 0.804 0.934
Acroparesthesia/Symptomatic 55 0.762 0.699 0.822
Single complication 18 0.744 0.658 0.821
Multiple complications  5 0.584 0.378 0.790
Total 97 0.772 0.729 0.815
  1. *Patients may contribute to more than one disease state.
  2. Given low patient numbers in the more progressive disease states, results were clustered by four states: asymptomatic, acroparesthesia/symptomatic, single complication, multiple complications. LCL: lower confidence limit. UCL: upper confidence limit.