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Table 3 Patient cohort by disease and age

From: The TREAT-NMD care and trial site registry: an online registry to facilitate clinical research for neuromuscular diseases

 

<18

18+

Total

DMD

8184

2203

10387

BMD

1301

1570

2871

Subtotal B/DMD

9485

3773

13258

SMA I

758

42

800

SMA II

1989

487

2476

SMA III

890

896

1786

Subtotal SMA

3637

1425

5062

LGMD

1630

3798

5428

CMD

918

221

1139

CM

947

418

1365

FSHD

586

2614

3200

DM1

1325

4718

6043

Subtotal Other

5406

11769

17175

Total

18528

16967

35495