Company | Date | Type | Disease | Registry | Geographic coverage |
---|---|---|---|---|---|
Prosensa | July 2009 | Feasibility enquiry | DMD | CTSR & PR | Europe, USA, Canada |
Acceleron | September 2009 | Feasibility enquiry | FSHD | CTSR only | Worldwide |
Trophos | March 2010 | Feasibility enquiry | SMA | CTSR & PR | Europe |
Acceleron | June 2010 | Feasibility enquiry | DMD | CTSR & PR | Europe, USA, Canada, Japan |
Santhera | December 2010 | Feasibility enquiry | DMD | CTSR & PR | Europe, USA, Canada |
Company X | November 2011 | Feasibility enquiry (refinement and update) | DMD | CTSR only | Worldwide |
Ultragenyx | November 2012 | Feasibility enquiry | GNE myopathy | CTSR only | Worldwide |
Eli Lilly | May 2013 | Feasibility enquiry | DMD | CTSR & PR | Worldwide |