From: Dysphagia as a risk factor for mortality in Niemann-Pick disease type C: systematic literature review and evidence from studies with miglustat
Death, n (%)
Untreated
Treated
n
(N = 97)
(N = 90)
Overall
74 (76)
3 (3)
Age category*
<2 years
27
27 (100)
4
0 (0)
2–11 years
48
40 (83)
37
2 (5)
>11 years
22
7 (32)
49
1 (2)