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Table 2 Median and mean survival of MPS I patients

From: The prevalence of and survival in Mucopolysaccharidosis I: Hurler, Hurler-Scheie and Scheie syndromes in the UK

  SURVIVAL (years)
  median (approximate 95% CI) mean (approximate 95% CI)
MPS I (ALL) 11.6 (9.5 to 13.7) 14.6 (13.0 to16.1)
HURLER (ALL) 8.7 (7.6 to 9.7) 10.5 (8.8 to12.2)
HURLER with censoring for BMT 6.8 (5.6 to 8.0) 6.6 (5.7 to 8.4)
HURLER that received BMT Can not estimate 15.6 (12.5 to 18.8)
HURLER that did not receive BMT 8.0 (7.0 to 8.9) 7.9 (7.0 to 8.8)
HURLER post-BMT survival Can not estimate 14.4 (11.5 to 17.4)
HURLER-SCHEIE Can not estimate 21.6 (19.3 to 24.0)
SCHEIE Can not estimate Can not estimate (1 death only)