A new framework for evaluating the health impacts of treatment for Gaucher disease type 1

Table 1 Generalized Estimating Equation Regression Results for Health State Utility in Gaucher Disease Type 1

	Mean or Proportion for estimation sample	Coefficient	Robust standard error	95% CI
DS3 Severity (vs. Mild)
Moderate	0.381	−0.078**	0.037	−0.150, −0.005
Marked	0.113	−0.122***	0.042	−0.205, −0.039
Severe	0.021	−0.168**	0.055	−0.275, −0.061
Bone Pain	0.258	−0.098***	0.034	−0.165, −0.032
Severe Skeletal Complications	0.103	0.018	0.037	−0.055, 0.090
Female	0.691	−0.049	0.030	−0.108, 0.010
Age at Treatment Initiation	53.9	−0.002*	0.001	−0.004, 0.001
Constant		0.880***	0.078	0.727, 1.033
Number of Observations	97
Number of Patients	50

ISSN: 1750-1172