From: Effectiveness of agalsidase alfa enzyme replacement in Fabry disease: cardiac outcomes after 10 years’ treatment
Females
Males
Left ventricular ejection fraction (%)
Baseline, mean (SD)
71.9 (7.6), n = 23
69.9 (7.3), n = 21
10-year n, mean (SD)
68.4 (6.9)
69.8 (7.0)
Change from baselinea
−3.64 (−6.74, −0.54)
1.31 (−2.16, 4.78)
p = 0.022
p =0.4546