Figure 1From: Miglustat therapy in the French cohort of paediatric patients with Niemann-Pick disease type CKey age milestones for NPC1 patients. Each horizontal bar represents age milestones for an individual patient. Data included only for NPC1 patient; *Patient 5 died aged 2 years and 9 months, and patient 12 died aged 13 years 11 months.Back to article page