| All patients (N = 42) |
---|---|
Demographics: | Â |
 Age, years, mean ± SD | 45.1 ± 12.7 |
 Gender, male: female, n | 22: 20 |
 Body weight, kg, mean ± SD | 76.7 ± 16.1 |
 Height in cm, mean ± SD | 169.9 ± 9.0 |
 Race, n (%): |  |
  Caucasian | 38 (90.5) |
  Asian | 1 (2.4) |
  Hispanic | 2 (4.8) |
  Other | 1 (2.4) |
Treatment history, mean ± SD: |  |
 Age at diagnosis, years | 24.8 ± 15.0 |
 Age at enzyme therapy initiation, years | 35.6 ± 12.5 |
 Duration of enzyme therapy, years | 9.5 ± 4.0 |
 Duration of current dose of enzyme therapy, years* | 4.9 ± 2.8 |
 Enzyme therapy dose at switch, IU/kg/month | 61.3 ± 35.7 |
Disease parameters, mean ± SD: |  |
 Liver volume in mL (n = 40) | 1726 ± 459.6 |
 Liver volume in MN (n = 40) | 0.91 ± 0.22 |
 Spleen volume†in mL (n = 30) | 484.7 ± 333.2 |
 Spleen volume†in MN (n = 30) | 3.13 ± 1.76 |
 Hemoglobin, g/dL (n = 41) | 14.89 ± 1.49 |
 Platelet count, × 109/L (n = 41) | 193.8 ± 92.06 |